Trials for cerebellar ataxias: from cellular models to human therapies
Éditeur :
Springer International Publishing AG
ISBN :
9783031243479
Date de publication :
30 mai 2024
Dimensions :
23,5 x 15,5 cm
Langue :
Anglais
Pays d'origine :
Suisse
The coverage begins by laying a foundation of the basic science of the cerebellum and ataxias, proceeds to discuss biomarkers and the tools of trials, offers guidelines on conducting trials, and then explores the full range of therapeutics and their trials, including gene therapy and cell transplantation.